Therapeutic Potential

RNA activation

Broad Therapeutic Potential

RaNA’s multi-dimensional approach enables the activation of the vast majority of genes, making our platform applicable to a broad range of diseases that have never had treatment options before now. The promise of RaNA’s platform for patients who have otherwise have had few or no approved treatment options is what makes us so fearless in our pursuits.


Programs in Discovery

While our technology has the potential to apply to a broad range of diseases, our initial focus is on genes repressed by disease, or genes where expression above normal levels would be therapeutically beneficial. Many such therapeutic areas exist, such as genetic, cardiovascular and metabolic, autoimmune, neurodegenerative, muscular and hematologic disease.